Preserving Ambulation in a Gene Therapy-Treated Girl Affected by Metachromatic Leukodystrophy: A Case Report

Preserving Ambulation in a Gene Therapy-Treated Girl Affected by Metachromatic Leukodystrophy: A Case Report

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Bibliographic Details
Published in:Journal of personalized medicine Vol. 13; no. 4
Main Authors: Faccioli, Silvia, Sassi, Silvia, Pandarese, Daniela, Borghi, Corrado, Montemaggiori, Valentina, Sarzana, Marina, Scarparo, Stefano, Butera, Carla, Calbi, Valeria, Aiuti, Alessandro, Fumagalli, Francesca
Format: Report
Language:English
Published: 06-04-2023
Online Access:Get full text
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Description
Bibliography:ObjectType-Case Study-2
content type line 59
SourceType-Reports-1
ObjectType-Report-1
ISSN:2075-4426
2075-4426
DOI:10.3390/jpm13040637