Search Results - "del Mar Municio, María"
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Safety and liver transduction efficacy of rAAV5-cohPBGD in nonhuman primates: a potential therapy for acute intermittent porphyria
Published in Human gene therapy (01-12-2013)“…Acute intermittent porphyria (AIP) results from haplo-insufficient activity of porphobilinogen deaminase (PBGD) and is characterized clinically by…”
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Non-clinical safety evaluation of AAV5-PBGD in mice and cynomolgus macaques
Published in Toxicology letters (28-08-2013)Get full text
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No longitudinal transmission of AAV5-PBGD vector DNA in mice
Published in Toxicology letters (28-08-2013)Get full text
Journal Article