Search Results - "Zaidman, Craig"

Muscle atrophy in mechanically-ventilated critically ill children by Johnson, Ryan W, Ng, Kay W P, Dietz, Alexander R, Hartman, Mary E, Baty, Jack D, Hasan, Nausheen, Zaidman, Craig M, Shoykhet, Michael

“…ICU-acquired muscle atrophy occurs commonly and worsens outcomes in adults. The incidence and severity of muscle atrophy in critically ill children are poorly…”
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Ultrasound in the Assessment of Myopathic Disorders by Zaidman, Craig M, van Alfen, Nens

“…Neuromuscular ultrasound (US) augments a careful physical examination and electrodiagnostic evaluation in the evaluation of suspected myopathy. Ultrasound…”
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Nerve size in chronic inflammatory demyelinating neuropathy varies with disease activity and therapy response over time: A retrospective ultrasound study by Zaidman, Craig M., Pestronk, Alan

“…ABSTRACT Introduction: Nerves are often enlarged in chronic inflammatory demyelinating polyneuropathy (CIDP). In this investigation we studied changes with…”
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Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial by Clemens, Paula R, Rao, Vamshi K, Connolly, Anne M, Harper, Amy D, Mah, Jean K, Smith, Edward C, McDonald, Craig M, Zaidman, Craig M, Morgenroth, Lauren P, Osaki, Hironori, Satou, Youhei, Yamashita, Taishi, Hoffman, Eric P

“…An unmet need remains for safe and efficacious treatments for Duchenne muscular dystrophy (DMD). To date, there are limited agents available that address the…”
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Peripheral nerve size in normals and patients with polyneuropathy: An ultrasound study by Zaidman, Craig M., Al-Lozi, Mohammed, Pestronk, Alan

“…Ultrasound has been used for visualizing peripheral nerve pathology. Our goal was to use ultrasound to quantitate the sizes of upper extremity nerves along…”
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Ultrasound of inherited vs. acquired demyelinating polyneuropathies by Zaidman, Craig M., Harms, Matthew B., Pestronk, Alan

“…We compared features of nerve enlargement in inherited and acquired demyelinating neuropathies using ultrasound. We measured median and ulnar nerve…”
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Nerve ultrasound in polyneuropathies by Telleman, Johan A., Grimm, Alexander, Goedee, Stephan, Visser, Leo H., Zaidman, Craig M.

“…ABSTRACT Ultrasound can be used to visualize pathology in the peripheral nerves of patients with polyneuropathy. Nerve enlargement is the most frequent…”
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Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy in patients with two copies of SMN2 (STR1VE): an open-label, single-arm, multicentre, phase 3 trial by Day, John W, Finkel, Richard S, Chiriboga, Claudia A, Connolly, Anne M, Crawford, Thomas O, Darras, Basil T, Iannaccone, Susan T, Kuntz, Nancy L, Peña, Loren D M, Shieh, Perry B, Smith, Edward C, Kwon, Jennifer M, Zaidman, Craig M, Schultz, Meredith, Feltner, Douglas E, Tauscher-Wisniewski, Sitra, Ouyang, Haojun, Chand, Deepa H, Sproule, Douglas M, Macek, Thomas A, Mendell, Jerry R

“…Spinal muscular atrophy type 1 is a motor neuron disorder resulting in death or the need for permanent ventilation by age 2 years. We aimed to evaluate the…”
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Electrical impedance myography for assessment of Duchenne muscular dystrophy by Rutkove, Seward B., Kapur, Kush, Zaidman, Craig M., Wu, Jim S., Pasternak, Amy, Madabusi, Lavanya, Yim, Sung, Pacheck, Adam, Szelag, Heather, Harrington, Tim, Darras, Basil T.

“…Objective Sensitive, objective, and easily applied methods for evaluating disease progression and response to therapy are needed for clinical trials in…”
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Onasemnogene abeparvovec for presymptomatic infants with two copies of SMN2 at risk for spinal muscular atrophy type 1: the Phase III SPR1NT trial by Strauss, Kevin A., Farrar, Michelle A., Muntoni, Francesco, Saito, Kayoko, Mendell, Jerry R., Servais, Laurent, McMillan, Hugh J., Finkel, Richard S., Swoboda, Kathryn J., Kwon, Jennifer M., Zaidman, Craig M., Chiriboga, Claudia A., Iannaccone, Susan T., Krueger, Jena M., Parsons, Julie A., Shieh, Perry B., Kavanagh, Sarah, Tauscher-Wisniewski, Sitra, McGill, Bryan E., Macek, Thomas A.

“…SPR1NT ( NCT03505099 ) was a Phase III, multicenter, single-arm study to investigate the efficacy and safety of onasemnogene abeparvovec for presymptomatic…”
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Onasemnogene abeparvovec for presymptomatic infants with three copies of SMN2 at risk for spinal muscular atrophy: the Phase III SPR1NT trial by Strauss, Kevin A., Farrar, Michelle A., Muntoni, Francesco, Saito, Kayoko, Mendell, Jerry R., Servais, Laurent, McMillan, Hugh J., Finkel, Richard S., Swoboda, Kathryn J., Kwon, Jennifer M., Zaidman, Craig M., Chiriboga, Claudia A., Iannaccone, Susan T., Krueger, Jena M., Parsons, Julie A., Shieh, Perry B., Kavanagh, Sarah, Wigderson, Melissa, Tauscher-Wisniewski, Sitra, McGill, Bryan E., Macek, Thomas A.

“…Most children with biallelic SMN1 deletions and three SMN2 copies develop spinal muscular atrophy (SMA) type 2. SPR1NT ( NCT03505099 ), a Phase III,…”
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Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series by Chand, Deepa H., Zaidman, Craig, Arya, Kapil, Millner, Rachel, Farrar, Michelle A., Mackie, Fiona E., Goedeker, Natalie L., Dharnidharka, Vikas R., Dandamudi, Raja, Reyna, Sandra P.

“…Spinal muscular atrophy is treated with onasemnogene abeparvovec, which replaces the missing survival motor neuron 1 gene via an adeno-associated virus vector…”
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Detection of peripheral nerve pathology: Comparison of ultrasound and MRI by Zaidman, Craig M, Seelig, Michael J, Baker, Jonathan C, Mackinnon, Susan E, Pestronk, Alan

“…OBJECTIVE:To compare accuracy of ultrasound and MRI for detecting focal peripheral nerve pathology, excluding idiopathic carpal or cubital tunnel syndromes…”
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Intramuscular blood flow in Duchenne and Becker Muscular Dystrophy: Quantitative power Doppler sonography relates to disease severity by Dietz, Alexander R., Connolly, Anne, Dori, Amir, Zaidman, Craig M.

“…•Post-exercise intramuscular blood flow is reduced in boys with Duchenne muscular dystrophy (DMD).•Reductions in intramuscular blood flow in Duchenne/Becker MD…”
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Quantitative muscle ultrasound detects disease progression in Duchenne muscular dystrophy by Zaidman, Craig M., Wu, Jim S., Kapur, Kush, Pasternak, Amy, Madabusi, Lavanya, Yim, Sung, Pacheck, Adam, Szelag, Heather, Harrington, Tim, Darras, Basil T., Rutkove, Seward B.

“…Objective We assessed changes in quantitative muscle ultrasound data in boys with Duchenne muscular dystrophy (DMD) and healthy controls to determine whether…”
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Immune-mediated myositis following gene therapy for Duchenne muscular dystrophy: a case report by Iannaccone, Susan T., Cai, Chunyu, Rhem, Brittney, Batley, Kaitlin, Rajaram, Veena, Greenberg, Benjamin M., Dharia, Sachi, Zaidman, Craig M.

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Intramuscular blood flow quantification with power doppler ultrasonography by Dori, Amir, Abbasi, Hiba, Zaidman, Craig M.

“…ABSTRACT Introduction Quantification of blood flow to muscle using ultrasound is limited to large vessels. Small vessel intramuscular blood flow cannot be…”
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Skeletal muscle imaging in neuromuscular disease by Simon, Neil G, Noto, Yu-ichi, Zaidman, Craig M

“…Highlights • Muscle ultrasound (US) and MRI are complementary to clinical and electrodiagnostic evaluation of neuromuscular disease. • US has benefits of…”
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Pulse oral corticosteroids in pediatric chronic inflammatory demyelinating polyneuropathy by Rogers, Amanda B., Zaidman, Craig M., Connolly, Anne M.

“…Childhood onset chronic inflammatory demyelinating polyneuropathy (CIDP) often requires long‐term immunomodulatory therapy. We report a comprehensive review of…”
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Muscle ultrasound quantifies disease progression over time in infants and young boys with duchenne muscular dystrophy by Zaidman, Craig M., Malkus, Elizabeth C., Connolly, Anne M.

“…ABSTRACT Introduction: Quantitative muscle ultrasound (QUS) in boys with Duchenne muscular dystrophy (DMD) shows increased echointensity as muscle is replaced…”
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