Search Results - "Thakrar, Sejal"

Muscle biopsies in clinical trials for Duchenne muscular dystrophy – Patients’ and caregivers’ perspective by Verhaart, Ingrid E.C., Johnson, Alex, Thakrar, Sejal, Vroom, Elizabeth, De Angelis, Fernanda, Muntoni, Francesco, Aartsma-Rus, Annemieke M., Niks, Erik H.

“…•Responders identified short term pain and long-term scarring as important impacts.•79% were little bothered about the scar, 21% were moderately or severely…”
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Measuring carer quality of life in Duchenne muscular dystrophy: a systematic review of the reliability and validity of self-report instruments using COSMIN by Carlton, Jill, Powell, Philip A

“…Duchenne muscular dystrophy is a rare, progressive, life-limiting genetic neuromuscular condition that significantly impacts the quality of life of informal…”
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Clinician Perspectives of Gene Therapy as a Treatment Option for Duchenne Muscular Dystrophy by Cope, Heidi, Fischer, Ryan, Heslop, Emma, McNiff, Megan, Johnson, Alexandra, Camino, Eric, Denger, Brian, Armstrong, Niki, Thakrar, Sejal, Bateman-House, Alison, Beaverson, Katherine L, Woollacott, Ione O C, Phillips, Dawn, Fernandez, Vivian, Ganot, Annie, Donisa-Dreghici, Roxana, Mansfield, Carol, Peay, Holly

“…Duchenne muscular dystrophy (DMD) is a progressive, life-limiting, neuromuscular disorder. Clinicians play an important role in informing families about…”
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