Search Results - "Sakkal, Aboud"

Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins by Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario

“…Targeted genome editing has a great therapeutic potential to treat disorders that require protein replacement therapy. To develop a platform independent of…”
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Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins by Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario

“…An amendment to this paper has been published and can be accessed via a link at the top of the paper…”
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Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor by Barbon, Elena, Kawecki, Charlotte, Marmier, Solenne, Sakkal, Aboud, Collaud, Fanny, Charles, Severine, Ronzitti, Giuseppe, Casari, Caterina, Christophe, Olivier, Denis, Cécile, Lenting, Peter J., Mingozzi, Federico

“…Abstract Von Willebrand disease (VWD), the most common inherited bleeding disorder in humans, is caused by quantitative or qualitative defects in von…”
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Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor by Barbon, Elena, Kawecki, Charlotte, Marmier, Solenne, Sakkal, Aboud, Collaud, Fanny, Charles, Severine, Ronzitti, Giuseppe, Casari, Caterina, Christophe, Olivier D., Denis, Cécile V., Lenting, Peter J., Mingozzi, Federico

“…Von Willebrand disease (VWD), the most common inherited bleeding disorder in humans, is caused by quantitative or qualitative defects in von Willebrand factor…”
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