Search Results - "Rocca, C. J"

Hematopoietic Stem Cells Transplantation Can Normalize Thyroid Function in a Cystinosis Mouse Model by Gaide Chevronnay, H. P, Janssens, V, Van Der Smissen, P, Rocca, C. J, Liao, X. H, Refetoff, S, Pierreux, C. E, Cherqui, S, Courtoy, P. J

“…Hypothyroidism is the most frequent and earliest endocrine complication in cystinosis, a multisystemic lysosomal storage disease caused by defective…”
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Gene Transfer to Mouse Kidney In Vivo by Rocca, C J, Cherqui, S

“…Genetic nephropathies represent a challenging class of disorders to be treated by gene therapy. This is primarily due to the filtering properties of the kidney…”
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rAAV9 combined with renal vein injection is optimal for kidney-targeted gene delivery: conclusion of a comparative study by Rocca, C J, Ur, S N, Harrison, F, Cherqui, S

“…Effective gene therapy strategies for the treatment of kidney disorders remain elusive. We report an optimized kidney-targeted gene delivery strategy using…”
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Molecular Evidence of Genome Editing in a Mouse Model of Immunodeficiency by Abdul-Razak, H. H., Rocca, C. J., Howe, S. J., Alonso-Ferrero, M. E., Wang, J., Gabriel, R., Bartholomae, C. C., Gan, C. H. V., Garín, M. I., Roberts, A., Blundell, M. P., Prakash, V., Molina-Estevez, F. J., Pantoglou, J., Guenechea, G., Holmes, M. C., Gregory, P. D., Kinnon, C., von Kalle, C., Schmidt, M., Bueren, J. A., Thrasher, A. J., Yáñez-Muñoz, R. J.

“…Genome editing is the introduction of directed modifications in the genome, a process boosted to therapeutic levels by designer nucleases. Building on the…”
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Europe's Trade; Study of Trade of European Countries with Each Other and with Rest of the World (Book Review) by Rocca, J C

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Raw Materials and Foodstuffs: Production by Countries, 1935 and 1938 (Book Review) by Rocca, J C

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Statistical Year Book of the League of Nations (Book Review) by Rocca, J C

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Money and Banking, 1939-40. I, Monetary Review (Book Review) by Rocca, J C

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The Last Spanish War: Revelations in “Diplomacy” by Rocca, J. C.

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Statistical Year-Book of League of Nations, 1938-1939 (Book Review) by Rocca, J C

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World Economic Survey, 1938-39 (Book Review) by Rocca, J C

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Review of World Trade, 1938 (Book Review) by Rocca, J C

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TINBERGEN, Method and Its Application to Investment Activity (Book Review) by Rocca, J C

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Money and Banking, 1938-39, I, II (Book Review) by Rocca, J C

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El Tratado Lozano-Salomon by Rocca, J. C.

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El Tratado Lozano-Salomon by Rocca, J. C., y Torrijos, Fabio Lozano

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The Last Spanish War: Revelations in "Diplomacy" by Rocca, J. C., Ferrara, Orestes, Shea, William E.

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