Search Results - "Moshkovich, Olga"
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Experiences of children and adolescents living with achondroplasia and their caregivers
Published in Molecular genetics & genomic medicine (01-04-2022)“…Background Achondroplasia, caused by a pathogenic variant in the fibroblast growth factor receptor 3 gene (FGFR3), leads to significant multisystem…”
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Challenges and Opportunities to Improve Cervical Cancer Screening Rates in US Health Centers through Patient-Centered Medical Home Transformation
Published in Advances in Preventive Medicine (01-01-2015)“…Over the last 50 years, the incidence of cervical cancer has dramatically decreased. However, health disparities in cervical cancer screening (CCS) persist for…”
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Content validation of a daily patient-reported outcome measure for assessing symptoms in patients with Small Intestinal Bacterial Overgrowth
Published in Quality of life research (01-09-2023)“…Purpose The aim of this study was to generate evidence supporting the development and content validity of a new PRO instrument, the Small Intestinal Bacterial…”
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Patient (pt) Experiences of Receiving Idecabtagene Vicleucel (Ide-Cel, bb2121) Versus Standard (Std) Regimens for the Treatment (Tx) of Relapsed/Refractory Multiple Myeloma (RRMM) in the Randomized, Controlled KarMMa-3 Clinical Trial: Analysis of Longitudinal Qualitative Interviews
Published in Blood (02-11-2023)“…Introduction: Ide-cel is a first-in-class B-cell maturation antigen (BCMA)-directed chimeric antigen receptor T cell therapy approved by the United States (US)…”
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Development of a signs and symptoms outcome measure for caregivers of patients with methylmalonic acidemia and propionic acidemia (MMAPAQ)
Published in Molecular genetics and metabolism (01-09-2024)“…Methylmalonic acidemia (MMA) and propionic acidemia (PA) are rare inborn errors of metabolism with shared signs and symptoms that are associated with…”
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Idecabtagene vicleucel (ide-cel, bb2121), a BCMA-directed CAR T-cell therapy: Qualitative analyses of pretreatment patient interviews in the KarMMa trial
Published in Journal of clinical oncology (10-10-2020)“…Abstract only 155 Background: Outcomes remain poor in triple-class exposed (to an immunomodulatory agent, a proteasome inhibitor, and an anti-CD38 antibody)…”
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Development of a conceptual model and patient-reported outcome measures for assessing symptoms and functioning in patients with heart failure
Published in Quality of life research (01-10-2020)“…Purpose Heart failure (HF) is a common condition that places considerable burden on patients. We aimed to develop a patient-reported outcome (PRO) measure to…”
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Idecabtagene Vicleucel (ide-cel, bb2121), a B-Cell Maturation Antigen-Directed Chimeric Antigen Receptor T Cell Therapy: Qualitative Analyses of Post-Treatment Interviews (Months 6-24) for Patients with Relapsed and Refractory Multiple Myeloma in the Karmma Clinical Trial
Published in Blood (23-11-2021)“…Introduction: Idecabtagene vicleucel (ide-cel), a B-cell maturation antigen (BCMA)-directed chimeric antigen receptor (CAR) T cell therapy, is approved by the…”
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Interviews of Patients (Pts) with Relapsed or Refractory (R/R) Large B-Cell Lymphoma (LBCL) Enrolled in 2 Lisocabtagene Maraleucel (liso-cel) Trials on Their Treatment Experience for 3 Months after Infusion
Published in Blood (23-11-2021)“…Pts with R/R LBCL had rapid and durable responses with liso-cel, a CD19-directed chimeric antigen receptor (CAR) T cell therapy. Previous qualitative research…”
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Analysis of patient-reported experiences up to 2 years after receiving idecabtagene vicleucel (ide-cel, bb2121) for relapsed or refractory multiple myeloma: Longitudinal findings from the phase 2 KarMMa trial
Published in Leukemia research (01-06-2023)“…To understand the long-term experience of patients receiving ide-cel chimeric antigen receptor T (CAR T) cell therapy for relapsed or refractory multiple…”
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Patient-Reported Experiences in Voxelotor-Treated Children and Adults with Sickle Cell Disease: A Semistructured Interview Study
Published in BioMed research international (2023)“…Objective. Voxelotor is a first-in-class sickle hemoglobin–polymerization inhibitor that was approved in 2019 by the US Food and Drug Administration for…”
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Development of a metabolic decompensation event severity score for patients with propionic acidemia or methylmalonic acidemia
Published in Molecular genetics and metabolism (01-04-2024)Get full text
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Correction to: Development of a conceptual model and patient-reported outcome measures for assessing symptoms and functioning in patients with heart failure
Published in Quality of life research (01-10-2020)“…The article Development of a conceptual model and patient-reported outcome measures for assessing symptoms and functioning in patients with heart failure…”
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Development of a conceptual model for variant late-infantile neuronal ceroid lipofuscinoses type 7 (CLN7)
Published in Molecular genetics and metabolism (01-02-2020)Get full text
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Qualitative Analysis of the Treatment Experience and Well-Being of Patients with Relapsed/Refractory (R/R) Large B-Cell Lymphoma (LBCL) Enrolled in 2 Trials of Lisocabtagene Maraleucel (liso-cel) during the Initial Stages of Therapy
Published in Blood (05-11-2020)“…Background: Chimeric antigen receptor (CAR) T cell therapy is a novel treatment modality for patients with R/R LBCL. Limited information exists regarding…”
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Patient experience before and after treatment with idecabtagene vicleucel (ide-cel, bb2121): qualitative analysis of patient interviews in the KarMMa trial
Published in Leukemia research (01-09-2022)“…To understand the experience of patients with relapsed and refractory multiple myeloma (RRMM) receiving idecabtagene vicleucel (ide-cel), a B-cell maturation…”
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Neurocognitive assessment platform for clinical trials in PKU: White paper developed by the NPKUA neurocognitive workgroup
Published in Molecular genetics and metabolism (01-09-2024)“…•This White Paper offers a neurocognitive assessment platform for clinical trials in PKU.•It describes 5 neuropsychological domains relevant to outcomes in…”
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eP140 - Experiences of individuals with achondroplasia and their caregivers: interim results from qualitative studies
Published in Molecular genetics and metabolism (01-04-2021)Get full text
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Experiences of individuals with achondroplasia and their caregivers: interim results from qualitative studies
Published in Molecular genetics and metabolism (01-04-2021)Get full text
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A New Measure Assessing Recovery from a Sickle Cell Crisis
Published in Blood (02-12-2016)“…Rationale: Vaso-occlusive crisis (VOC) is a recurring complication of sickle cell disease (SCD) and a common reason for emergency department visits and…”
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