Search Results - "Melere, M"

OC7 Maralixibat-treated patients with Alagille syndrome demonstrate event-free survival in a natural history comparison with patients with from the GALA database: application of real-world evidence analytics by Hansen, B E, Vandriel, S M, Vig, P, Garner, W, Mogul, D B, Loomes, K M, Piccoli, DA, Rand, E B, Jankowska, I, Czubkowski, P, Gliwicz-Miedzińska, D, Gonzales, E M, Jacquemin, E, Bouligand, J, L D’Antiga, Nicastro, E, Arnell, H, Fischler, B, Sokal, É, Demaret, T, Siew, S, Stormon, M, Karpen, S J, Romero, R, Ebel, N H, Feinstein, JA, Roberts, A J, Evans, H M, Sundaram, S S, Chaidez, A, Hardikar, W, Shankar, S, Fischer, R T, Lacaille, F, Debray, D, Lin, H C, Jensen, M K, Jaramillo, C, Karthikeyan, P, Indolfi, G, Verkade, HJ, Larson-Nath, C, Quiros-Tejeira, R E, Valentino, P L, Rogalidou, M, Dezsőfi, A, Squires, JE, Schwarz, K, Calvo, P L, J Quintero Bernabeu, Zizzo, AN, Nebbia, G, Bulut, P, Santos-Silva, E, Fawaz, R, Nastasio, S, Karnsakul, W, M Legarda Tamara, C Molera Busoms, Kelly, D, T Damgaard Sandahl, Jimenez-Rivera, C, Banales, JM, Mujawar, Q, Li, L T, She, H, Wang, J S, Kim, K M, Oh, SH, Sanchez, M C, Cavalieri, M L, Lee, W S, Hajinicolaou, C, Lertudomphonwanit, C, Waisbourd-Zinman, O, Arikan, C, Alam, S, Carvalho, E, Melere, M, Eshun, J, Önal, Z, Desai, D M, Wiecek, S, Pinto, R B, Wolters, V M, Garcia, J, Beretta, M, Kerkar, N, Brecelj, J, Rock, N, Lurz, E, Blondet, N, Shah, U, Thompson, R J, Kamath, B M

“…Real-world evidence (RWE) analytics continue to advance natural history comparisons in rare diseases. The Global Alagille Alliance (GALA) is the largest global…”
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CLINICAL FEATURES AND OUTCOMES IN AN INTERNATIONAL COHORT OF 731 ALAGILLE SYNDROME PATIENTS FROM 19 COUNTRIES by Vandriel, S, Wang, JS, Li, LT, Piccoli, DA, Loomes, KM, Sokal, EM, Demaret, T, Arnell, H, Fischler, B, Fawaz, RL, Nastasio, S, Hardikar, W, Shankar, S, Lee, WS, Lertudomphonwanit, C, Karnsakul, W, Karpen, SJ, Fischer, RT, Quiros, RE, Melere, M, Bujanda, L, Indolfi, G, Nicastro, E, Calvo, PL, Valentino, PL, Schwarz, KB, Kanavaki, I, Dezsofi, A, Mujawar, Q, Pinto, RB, Brecelj, J, Kerkar, N, Sanchez, MC, Karthikeyan, P, Santos-Silva, E, Jimenez-Rivera, C, Mozer-Glassberg, Y, Alam, S, Hansen, BE, Kamath, BM

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