Search Results - "Manno, Catherine"

Sirolimus is effective in relapsed/refractory autoimmune cytopenias: results of a prospective multi-institutional trial by Bride, Karen L., Vincent, Tiffaney, Smith-Whitley, Kim, Lambert, Michele P., Bleesing, Jack J., Seif, Alix E., Manno, Catherine S., Casper, James, Grupp, Stephan A., Teachey, David T.

“…Patients with autoimmune multilineage cytopenias are often refractory to standard therapies requiring chronic immunosuppression with medications with limited…”
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Modern management of haemophilic arthropathy by Leslie, Raffini, Catherine, Manno

“…Summary Currently available factor concentrates for treatment of patients with haemophilia are virally inactivated or are made by recombinant technology and…”
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The Growth of Regional Children's Campuses and Academic Departments of Pediatrics by Steiner, Michael J., Moya, Fernando, Liles, Bethany L., Jaskolka, Michael, Pino, Joseph, Hurtado, Christine Waasdorp, Manno, Catherine S., Davis, Stephanie D.

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Leadership Development Program Outcomes by Davies, H. Dele, Degnon, Laura E., Donavan, Sarah K., Wilmott, Robert W., Manno, Catherine S.

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CD8 + T-cell responses to adeno-associated virus capsid in humans by High, Katherine A, Mingozzi, Federico, Maus, Marcela V, Hui, Daniel J, Sabatino, Denise E, Murphy, Samuel L, Rasko, John E J, Ragni, Margaret V, Manno, Catherine S, Sommer, Jurg, Jiang, Haiyan, Pierce, Glenn F, Ertl, Hildegund C J

“…Hepatic adeno-associated virus (AAV)-serotype 2 mediatedgene transfer results in transgene product expression that is sustained in experimental animals but not…”
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Associations between intracranial haemorrhage and prescribed prophylaxis in a large cohort of haemophilia patients in the United States by Witmer, Char, Presley, Rodney, Kulkarni, Roshni, Michael Soucie, J., Manno, Catherine S., Raffini, Leslie

“…Summary Intracranial haemorrhage (ICH) is the most serious type of bleeding for patients with haemophilia. Prior published reports regarding ICH predate the…”
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Identifying autoimmune lymphoproliferative syndrome in children with Evans syndrome: a multi-institutional study by Seif, Alix E., Manno, Catherine S., Sheen, Cecilia, Grupp, Stephan A., Teachey, David T.

“…Autoimmune lymphoproliferative syndrome (ALPS) is a disorder of abnormal lymphocyte survival caused by dysregulation of the Fas apoptotic pathway. Clinical…”
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Characteristics of Hospitalized Children With SARS-CoV-2 in the New York City Metropolitan Area by Verma, Sourabh, Lumba, Rishi, Dapul, Heda M, Gold-von Simson, Gabrielle, Phoon, Colin K, Lighter, Jennifer L, Farkas, Jonathan S, Vinci, Alexandra, Noor, Asif, Raabe, Vanessa N, Rhee, David, Rigaud, Mona, Mally, Pradeep V, Randis, Tara M, Dreyer, Benard, Ratner, Adam J, Manno, Catherine S, Chopra, Arun

“…To describe the characteristics of hospitalized children with severe acute respiratory syndrome coronavirus 2 in New York City metropolitan area. This was a…”
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Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B by Jiang, Haiyan, Pierce, Glenn F, Ozelo, Margareth C, de Paula, Erich V, Vargas, Joseph A, Smith, Peter, Sommer, Jürg, Luk, Alvin, Manno, Catherine S, High, Katherine A, Arruda, Valder R

“…In a phase I study, administration of an AAV2-FIX vector into the skeletal muscle of eight hemophilia B subjects proved safe and achieved local gene transfer…”
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Pediatric Hematology by Manno, Catherine S., MD

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AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B by Manno, Catherine S., Chew, Amy J., Hutchison, Sylvia, Larson, Peter J., Herzog, Roland W., Arruda, Valder R., Tai, Shing Jen, Ragni, Margaret V., Thompson, Arthur, Ozelo, Margareth, Couto, Linda B., Leonard, Debra G.B., Johnson, Frederick A., McClelland, Alan, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W., Kay, Mark A., High, Katherine A., Glader, Bertil

“…Hemophilia B is an X-linked coagulopathy caused by absence of functional coagulation factor IX (F.IX). Previously, we established an experimental basis for…”
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Incidence of Bleeding Complications in Pediatric Patients with Type 1 von Willebrand Disease Undergoing Adenotonsillar Procedures by Witmer, Char M., MD, Elden, Lisa, MD, Butler, Regina B., RN, Manno, Catherine S., MD, Raffini, Leslie J., MD

“…Objective To review the incidence of postoperative bleeding in children with type 1 von Willebrand disease (VWD) who were treated with a single institution…”
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Dose of Prophylactic Platelet Transfusions and Prevention of Hemorrhage by Slichter, Sherrill J, Kaufman, Richard M, Assmann, Susan F, McCullough, Jeffrey, Triulzi, Darrell J, Strauss, Ronald G, Gernsheimer, Terry B, Ness, Paul M, Brecher, Mark E, Josephson, Cassandra D, Konkle, Barbara A, Woodson, Robert D, Ortel, Thomas L, Hillyer, Christopher D, Skerrett, Donna L, McCrae, Keith R, Sloan, Steven R, Uhl, Lynne, George, James N, Aquino, Victor M, Manno, Catherine S, McFarland, Janice G, Hess, John R, Leissinger, Cindy, Granger, Suzanne

“…The use of platelet transfusions to prevent bleeding in patients with thrombocytopenia due to chemotherapy or other causes of marrow suppression is widespread,…”
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Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector by High, Katherine A, Kay, Mark A, Manno, Catherine S, Ragni, Margaret V, Larson, Peter J, Couto, Linda B, McClelland, Alan, Glader, Bertil, Chew, Amy J, J Tai, Shing, Herzog, Roland W, Arruda, Valder, Johnson, Fred, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W

“…Pre-clinical studies in mice and haemophilic dogs have shown that introduction of an adeno-associated viral (AAV) vector encoding blood coagulation factor IX…”
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Unmasking Evans syndrome: T-cell phenotype and apoptotic response reveal autoimmune lymphoproliferative syndrome (ALPS) by Teachey, David T., Manno, Catherine S., Axsom, Kelly M., Andrews, Timothy, Choi, John K., Greenbaum, Barbara H., McMann, Joseph M., Sullivan, Kathleen E., Travis, Susan F., Grupp, Stephan A.

“…Autoimmune lymphoproliferative syndrome (ALPS) is a rare disorder of disrupted lymphocyte homeostasis. Clinical manifestations of ALPS vary but typically…”
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Rapamycin improves lymphoproliferative disease in murine autoimmune lymphoproliferative syndrome (ALPS) by Teachey, David T., Obzut, Dana A., Axsom, Kelly, Choi, John K., Goldsmith, Kelly C., Hall, Junior, Hulitt, Jessica, Manno, Catherine S., Maris, John M., Rhodin, Nicholas, Sullivan, Kathleen E., Brown, Valerie I., Grupp, Stephan A.

“…Autoimmune lymphoproliferative syndrome (ALPS) is a disorder of abnormal lymphocyte survival caused by defective Fas-mediated apoptosis, leading to…”
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Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response by High, Katherine A, Manno, Catherine S, Pierce, Glenn F, Arruda, Valder R, Glader, Bertil, Ragni, Margaret, Rasko, John J E, Ozelo, Margareth C, Hoots, Keith, Blatt, Philip, Konkle, Barbara, Dake, Michael, Kaye, Robin, Razavi, Mahmood, Zajko, Albert, Zehnder, James, Rustagi, Pradip, Nakai, Hiroyuki, Chew, Amy, Leonard, Debra, Wright, J Fraser, Lessard, Ruth R, Sommer, Jürg M, Tigges, Michael, Sabatino, Denise, Luk, Alvin, Jiang, Haiyan, Mingozzi, Federico, Couto, Linda, Ertl, Hildegund C, Kay, Mark A

“…We have previously shown that a single portal vein infusion of a recombinant adeno-associated viral vector (rAAV) expressing canine Factor IX (F.IX) resulted…”
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A prospective observational study of IVC filters in pediatric patients by Raffini, Leslie, Cahill, Anne Marie, Hellinger, Jeffrey, Manno, Catherine

“…Background The use of inferior vena cava (IVC) filters to prevent pulmonary embolism (PE) has increased with the advent of retrievable filters (Crowther: Am J…”
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Treatment with sirolimus ameliorates tacrolimus-induced autoimmune cytopenias after solid organ transplant by Teachey, David T., Jubelirer, Tracey, Baluarte, H. Jorge, Wade, Amanda, Manno, Catherine S.

“…The development of autoimmune blood cell cytopenias is a potentially life‐threatening complication of solid organ transplantation, resulting from T‐cell…”
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Guidelines for assessing appropriateness of pediatric transfusion by Roseff, Susan D., Luban, Naomi L.C., Manno, Catherine S.

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