Search Results - "Liao, Sophia H Y"

  • Showing 1 - 13 results of 13
Refine Results
  1. 1
  2. 2
  3. 3
  4. 4
  5. 5

    Development of CNS tropic AAV1-like variants with reduced liver-targeting following systemic administration in mice by Drouyer, Matthieu, Merjane, Jessica, Nazareth, Deborah, Knight, Maddison, Scott, Suzanne, Liao, Sophia H Y, Ginn, Samantha L, Zhu, Erhua, Alexander, Ian E, Lisowski, Leszek

    Published in Molecular therapy (06-03-2024)
    “…Directed evolution of natural AAV9 using peptide display libraries have been widely used in the search for an optimal recombinant AAV (rAAV) for transgene…”
    Get more information
    Journal Article
  6. 6
  7. 7
  8. 8
  9. 9
  10. 10
  11. 11

    Efficient in vivo editing of OTC-deficient patient-derived primary human hepatocytes by Ginn, Samantha L., Amaya, Anais K., Liao, Sophia H.Y., Zhu, Erhua, Cunningham, Sharon C., Lee, Michael, Hallwirth, Claus V., Logan, Grant J., Tay, Szun S., Cesare, Anthony J., Pickett, Hilda A., Grompe, Markus, Dilworth, Kimberley, Lisowski, Leszek, Alexander, Ian E.

    Published in JHEP reports (01-02-2020)
    “…Genome editing technology has immense therapeutic potential and is likely to rapidly supplant contemporary gene addition approaches. Key advantages include the…”
    Get full text
    Journal Article
  12. 12

    Lymphomagenesis in SCID-X1 Mice Following Lentivirus-mediated Phenotype Correction Independent of Insertional Mutagenesis and γc Overexpression by Ginn, Samantha L, Liao, Sophia HY, Dane, Allison P, Hu, Min, Hyman, Jessica, Finnie, John W, Zheng, Maolin, Cavazzana-Calvo, Marina, Alexander, Stephen I, Thrasher, Adrian J, Alexander, Ian E

    Published in Molecular therapy (01-05-2010)
    “…The development of leukemia as a consequence of vector-mediated genotoxicity in gene therapy trials for X-linked severe combined immunodeficiency (SCID-X1) has…”
    Get full text
    Journal Article
  13. 13

    Lymphomagenesis in SCID-X1 mice following lentivirus-mediated phenotype correction independent of insertional mutagenesis and gammac overexpression by Ginn, Samantha L, Liao, Sophia H Y, Dane, Allison P, Hu, Min, Hyman, Jessica, Finnie, John W, Zheng, Maolin, Cavazzana-Calvo, Marina, Alexander, Stephen I, Thrasher, Adrian J, Alexander, Ian E

    Published in Molecular therapy (01-05-2010)
    “…The development of leukemia as a consequence of vector-mediated genotoxicity in gene therapy trials for X-linked severe combined immunodeficiency (SCID-X1) has…”
    Get full text
    Journal Article