Search Results - "KANTER, Julie"
-
1
A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease
Published in The New England journal of medicine (08-08-2019)“…In a trial evaluating two daily-dose levels of voxelotor, which binds to sickle hemoglobin and prevents polymerization under hypoxic conditions, hemoglobin…”
Get full text
Journal Article -
2
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease
Published in The New England journal of medicine (17-02-2022)“…An unprespecified interim analysis of results from a phase 1–2 study of gene therapy for sickle cell disease shows resolution of severe vaso-occlusive events…”
Get full text
Journal Article -
3
Crizanlizumab for the Prevention of Pain Crises in Sickle Cell Disease
Published in The New England journal of medicine (02-02-2017)“…In this yearlong trial involving patients with sickle cell disease, crizanlizumab, an antibody to P-selectin, was associated with a 45% lower rate of pain…”
Get full text
Journal Article -
4
Challenges to Management of Pain in Sickle Cell Disease
Published in Thalassemia reports (01-04-2018)“…Sickle Cell Disease (SCD) is one of the most common blood disorders in the world. Pain is the primary reason for which individuals with SCD interact with the…”
Get full text
Journal Article -
5
Perspectives of individuals with sickle cell disease on barriers to care
Published in PloS one (23-03-2022)“…Sickle cell disease (SCD) is an inherited hemoglobinopathy that predominantly affects African Americans in the United States. The disease is associated with…”
Get full text
Journal Article -
6
Salvage therapy of refractory hemophagocytic lymphohistiocytosis with alemtuzumab
Published in Pediatric blood & cancer (01-01-2013)“…Background Hemophagocytic lymphohistiocytosis (HLH) is a life‐threatening hyperinflammatory syndrome that remains difficult to treat. Even with current…”
Get full text
Journal Article -
7
Current and novel therapies for the prevention of vaso-occlusive crisis in sickle cell disease
Published in Therapeutic Advances in Hematology (2020)“…Individuals with sickle cell disease (SCD) are living further into adulthood in high-resource countries. However, despite increased quantity of life,…”
Get full text
Book Review Journal Article -
8
Density-based separation in multiphase systems provides a simple method to identify sickle cell disease
Published in Proceedings of the National Academy of Sciences - PNAS (14-10-2014)“…Significance Red blood cells with a high density (ρ > 1.120 g/cm ³) are characteristic of sickle cell disease. This paper demonstrates a density-based…”
Get full text
Journal Article -
9
Lovo‐cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB‐206 study
Published in American journal of hematology (01-01-2023)“…lovo‐cel (bb1111; LentiGlobin for sickle cell disease [SCD]) gene therapy (GT) comprises autologous transplantation of hematopoietic stem and progenitor cells…”
Get full text
Journal Article -
10
Factors associated with left ventricular hypertrophy in children with sickle cell disease; results from the DISPLACE study
Published in Haematologica (Roma) (01-10-2022)“…Cardiopulmonary complications remain a leading cause of morbidity and mortality in sickle cell disease (SCD). The overall goals of this study were to evaluate…”
Get full text
Journal Article -
11
Sex-based differences in the manifestations and complications of sickle cell disease: Report from the Sickle Cell Disease Implementation Consortium
Published in PloS one (29-10-2021)“…Sex-based clinical outcome differences in sickle cell disease (SCD) remain largely unknown despite evidence that female sex is associated with an increased…”
Get full text
Journal Article -
12
48847 Assessing Transition Outcomes in Sickle Cell Disease (SCD) Prior To Implementation of A Formal Transition Program
Published in Journal of clinical and translational science (01-03-2021)“…ABSTRACT IMPACT: To identify potential facilitators and barriers to a successful transition in care. OBJECTIVES/GOALS: Improvements in care for children with…”
Get full text
Journal Article -
13
Current Methods of Newborn Screening Follow-Up for Sickle Cell Disease Are Highly Variable and without Quality Assurance: Results from the ENHANCE Study
Published in International journal of neonatal screening (01-03-2024)“…Newborn screening (NBS) for sickle cell disease (SCD) has significantly improved childhood survival but there are still gaps resulting in delayed care for…”
Get full text
Journal Article -
14
Simple paper-based test for measuring blood hemoglobin concentration in resource-limited settings
Published in Clinical chemistry (Baltimore, Md.) (01-10-2013)“…The measurement of hemoglobin concentration ([Hb]) is performed routinely as a part of a complete blood cell count to evaluate the oxygen-carrying capacity of…”
Get full text
Journal Article -
15
Publication of data collection forms from NHLBI funded sickle cell disease implementation consortium (SCDIC) registry
Published in Orphanet journal of rare diseases (07-07-2020)“…Sickle cell disease (SCD) is an autosomal recessive blood disorder affecting approximately 100,000 Americans and 3.1 million people globally. The scarcity of…”
Get full text
Journal Article -
16
Identifying barriers to evidence-based care for sickle cell disease: results from the Sickle Cell Disease Implementation Consortium cross-sectional survey of healthcare providers in the USA
Published in BMJ open (17-11-2021)“…ObjectivesSickle cell disease (SCD) leads to chronic and acute complications that require specialised care to manage symptoms and optimise clinical results…”
Get full text
Journal Article -
17
Validation of a Low-Cost Paper-Based Screening Test for Sickle Cell Anemia
Published in PloS one (06-01-2016)“…The high childhood mortality and life-long complications associated with sickle cell anemia (SCA) in developing countries could be significantly reduced with…”
Get full text
Journal Article -
18
Social determinants of health and treatment center affiliation: analysis from the sickle cell disease implementation consortium registry
Published in BMC health services research (06-03-2024)“…Adults with sickle cell disease (SCD) suffer early mortality and high morbidity. Many are not affiliated with SCD centers, defined as no ambulatory visit with…”
Get full text
Journal Article -
19
-
20
Association Between Patent Foramen Ovale and Overt Ischemic Stroke in Children With Sickle Cell Disease
Published in Frontiers in neurology (13-12-2021)“…Ischemic stroke is one of the most devastating complications of sickle cell anemia (SCA). Previous studies have shown that intracardiac shunting including…”
Get full text
Journal Article