Search Results - "Holuba, N"
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G.O.18
Published in Neuromuscular disorders : NMD (01-10-2014)“…This open-label, multiple ascending-dose study was conducted to evaluate the safety, tolerability, pharmacokinetics, pharmacodynamics, and efficacy of…”
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Pediatrics-1 Spinal Muscular Atrophy Type I: Cases of Normal Cognitive Function Despite having Limited Motor Function and Physical-Environmental Interaction
Published in Archives of clinical neuropsychology (01-09-2015)“…Objective: To examine cognitive development in children with Spinal Muscular Atrophy Type 1 (SMA 1 ), a population with extremely limited motor function. SMA…”
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G.O.18: Results of a phase 2 study of ISIS-SMNRx in children with spinal muscular atrophy
Published in Neuromuscular disorders : NMD (01-10-2014)“…This open-label, multiple ascending-dose study was conducted to evaluate the safety, tolerability, pharmacokinetics, pharmacodynamics, and efficacy of…”
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