Search Results - "Goubin, H"
-
1
P.20.12 Gene therapy of Duchenne Muscular Dystrophy using rAAV vectors: Patterns of dystrophin expression and histological improvements
Published in Neuromuscular disorders : NMD (01-10-2013)“…Duchenne Muscular Dystrophy (DMD) is caused by mutations in the gene encoding dystrophin. About 60% of the affected boys are treatable by exon skipping, i.e…”
Get full text
Journal Article -
2
G.P.92
Published in Neuromuscular disorders : NMD (01-10-2014)“…We have previously demonstrated that a recombinant adeno-associated virus vector, serotype 8 (rAAV8) carrying a modified U7snRNA sequence promoting exon…”
Get full text
Journal Article -
3
G.P.92 : Persistence and stability at 6 months of AAV genome and dystrophin expression in GRMD dogs after forelimb delivery of a recombinant AAV carrying an exon skipping sequence
Published in Neuromuscular disorders : NMD (01-10-2014)“…We have previously demonstrated that a recombinant adeno-associated virus vector, serotype 8 (rAAV8) carrying a modified U7snRNA sequence promoting exon…”
Get full text
Journal Article