Search Results - "Foust, K.D"
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Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Published in The New England journal of medicine (02-11-2017)Get full text
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AVXS-101 Phase 1 gene therapy clinical trial in SMA Type 1: Interim data demonstrates improvements in supportive care use
Published in European journal of paediatric neurology (01-06-2017)Get full text
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3
AVXS-101 Phase 1 gene therapy clinical trial in SMA Type 1: Event free survival and achievement of developmental milestones
Published in European journal of paediatric neurology (01-06-2017)Get full text
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4
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Published in The New England journal of medicine (02-11-2017)“…Fifteen children with spinal muscular atrophy type 1 received gene-replacement therapy with a single dose of adeno-associated virus containing SMN. In marked…”
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Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes
Published in Nature medicine (01-02-2009)Get full text
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Gene delivery to the spinal cord using MRI-guided focused ultrasound
Published in Gene therapy (01-07-2015)“…Non-invasive gene delivery across the blood–spinal cord barrier (BSCB) remains a challenge for treatment of spinal cord injury and disease. Here, we…”
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